Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study

Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study

Bibliographic Details
Main Authors:	Suhr, Ole B, Coelho, Teresa, Buades, Juan, Pouget, Jean, Conceicao, Isabel, Berk, John, Schmidt, Hartmut, Waddington-Cruz, Márcia, Campistol, Josep M., Bettencourt, Brian R., Vaishnaw, Akshay, Gollob, Jared, Adams, David
Format:	Online
Language:	English
Published:	BioMed Central 2015
Online Access:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4559363/

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