When to decide to enroll a TTR-FAP patient in a Clinical Trial?

by Buades, Juan
Published 2015

Preliminary assessment of neuropathy progression in patients with hereditary ATTR amyloidosis after orthotopic liver transplantation (OLT)

by Adams, David, Buades, Juan, Suhr, Ole, Obici, Laura, Coelho, Teresa
Published 2015

Recommendations for presymptomatic genetic testing and management of individuals at risk for hereditary transthyretin amyloidosis

by Obici, Laura, Kuks, Jan B., Buades, Juan, Adams, David, Suhr, Ole B., Coelho, Teresa, Kyriakides, Theodore
Published 2016

Phase 2 open-label extention (OLE) study of patisiran, an investigational siRNA agent for familial amyloidotic polyneuropathy (FAP)

by Adams, David, Suhr, Ole B, Conceicao, Isabel, Waddington-Cruz, Marcia, Schmidt, Hartmut, Buades, Juan, Campistol, Josep, Coehlo, Teresa
Published 2015

Cardiac extracellular volume quantified with T1 mapping techniques reflects degree of cardiac and neurological involvement in Hereditary Transthyretin Amyloidosis

by González-López, Esther, Gallego-Delgado, María, Muñoz-Beamud, Francisco, Buades, Juan, Galán, Lucía, Blanco, Jose Luis Muñoz, González-Mirelis, Jesús, García-Pavía, Pablo
Published 2015

Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study

by Suhr, Ole B, Coelho, Teresa, Buades, Juan, Pouget, Jean, Conceicao, Isabel, Berk, John, Schmidt, Hartmut, Waddington-Cruz, Márcia, Campistol, Josep M., Bettencourt, Brian R., Vaishnaw, Akshay, Gollob, Jared, Adams, David
Published 2015