Inactivation of Hepatitis B Virus Replication in Cultured Cells and In Vivo with Engineered Transcription Activator-Like Effector Nucleases

by Bloom, Kristie, Ely, Abdullah, Mussolino, Claudio, Cathomen, Toni, Arbuthnot, Patrick
Published 2013

A novel TALE nuclease scaffold enables high genome editing activity in combination with low toxicity

by Mussolino, Claudio, Morbitzer, Robert, Lütge, Fabienne, Dannemann, Nadine, Lahaye, Thomas, Cathomen, Toni
Published 2011

Zinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosa

by Mussolino, Claudio, Sanges, Daniela, Marrocco, Elena, Bonetti, Ciro, Di Vicino, Umberto, Marigo, Valeria, Auricchio, Alberto, Meroni, Germana, Surace, Enrico Maria
Published 2011

TALENs facilitate targeted genome editing in human cells with high specificity and low cytotoxicity

by Mussolino, Claudio, Alzubi, Jamal, Fine, Eli J., Morbitzer, Robert, Cradick, Thomas J., Lahaye, Thomas, Bao, Gang, Cathomen, Toni
Published 2014

Engineered zinc finger nickases induce homology-directed repair with reduced mutagenic effects

by Ramirez, Cherie L., Certo, Michael T., Mussolino, Claudio, Goodwin, Mathew J., Cradick, Thomas J., McCaffrey, Anton P., Cathomen, Toni, Scharenberg, Andrew M., Joung, J. Keith
Published 2012

Differential integrity of TALE nuclease genes following adenoviral and lentiviral vector gene transfer into human cells

by Holkers, Maarten, Maggio, Ignazio, Liu, Jin, Janssen, Josephine M., Miselli, Francesca, Mussolino, Claudio, Recchia, Alessandra, Cathomen, Toni, Gonçalves, Manuel A. F. V.
Published 2013

Improved bi-allelic modification of a transcriptionally silent locus in patient-derived iPSC by Cas9 nickase

by Eggenschwiler, Reto, Moslem, Mohsen, Fráguas, Mariane Serra, Galla, Melanie, Papp, Oliver, Naujock, Maximilian, Fonfara, Ines, Gensch, Ingrid, Wähner, Annabell, Beh-Pajooh, Abbas, Mussolino, Claudio, Tauscher, Marcel, Steinemann, Doris, Wegner, Florian, Petri, Susanne, Schambach, Axel, Charpentier, Emmanuelle, Cathomen, Toni, Cantz, Tobias
Published 2016

Rescue of DNA-PK Signaling and T-Cell Differentiation by Targeted Genome Editing in a prkdc Deficient iPSC Disease Model

by Rahman, Shamim H., Kuehle, Johannes, Reimann, Christian, Mlambo, Tafadzwa, Alzubi, Jamal, Maeder, Morgan L., Riedel, Heimo, Fisch, Paul, Cantz, Tobias, Rudolph, Cornelia, Mussolino, Claudio, Joung, J. Keith, Schambach, Axel, Cathomen, Toni
Published 2015