Zinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosa

by Mussolino, Claudio, Sanges, Daniela, Marrocco, Elena, Bonetti, Ciro, Di Vicino, Umberto, Marigo, Valeria, Auricchio, Alberto, Meroni, Germana, Surace, Enrico Maria
Published 2011

Myosin7a Deficiency Results in Reduced Retinal Activity Which Is Improved by Gene Therapy

by Colella, Pasqualina, Sommella, Andrea, Marrocco, Elena, Di Vicino, Umberto, Polishchuk, Elena, Garrido, Marina Garcia, Seeliger, Mathias W., Polishchuk, Roman, Auricchio, Alberto
Published 2013

Effective delivery of large genes to the retina by dual AAV vectors

by Trapani, Ivana, Colella, Pasqualina, Sommella, Andrea, Iodice, Carolina, Cesi, Giulia, de Simone, Sonia, Marrocco, Elena, Rossi, Settimio, Giunti, Massimo, Palfi, Arpad, Farrar, Gwyneth J, Polishchuk, Roman, Auricchio, Alberto
Published 2014

MicroRNA-Restricted Transgene Expression in the Retina

by Karali, Marianthi, Manfredi, Anna, Puppo, Agostina, Marrocco, Elena, Gargiulo, Annagiusi, Allocca, Mariacarmela, Corte, Michele Della, Rossi, Settimio, Giunti, Massimo, Bacci, Maria Laura, Simonelli, Francesca, Surace, Enrico Maria, Banfi, Sandro, Auricchio, Alberto
Published 2011

Recombinant Vectors Based on Porcine Adeno-Associated Viral Serotypes Transduce the Murine and Pig Retina

by Puppo, Agostina, Bello, Alexander, Manfredi, Anna, Cesi, Giulia, Marrocco, Elena, Corte, Michele Della, Rossi, Settimio, Giunti, Massimo, Bacci, Maria Laura, Simonelli, Francesca, Surace, Enrico Maria, Kobinger, Gary P., Auricchio, Alberto
Published 2013

Rhodopsin targeted transcriptional silencing by DNA-binding

by Botta, Salvatore, Marrocco, Elena, de Prisco, Nicola, Curion, Fabiola, Renda, Mario, Sofia, Martina, Lupo, Mariangela, Carissimo, Annamaria, Bacci, Maria Laura, Gesualdo, Carlo, Rossi, Settimio, Simonelli, Francesca, Surace, Enrico Maria
Published 2016

Retinal transduction profiles by high-capacity viral vectors

by Puppo, Agostina, Cesi, Giulia, Marrocco, Elena, Piccolo, Pasquale, Jacca, Sarah, Shayakhmetov, Dmitry M., Parks, Robin J., Davidson, Beverly L., Colloca, Stefano, Brunetti-Pierri, Nicola, Ng, Philip, Donofrio, Gaetano, Auricchio, Alberto
Published 2014