Quantitative Analysis of α-L-Iduronidase Expression in Immunocompetent Mice Treated with the Sleeping Beauty Transposon System

by Aronovich, Elena L., Hall, Bryan C., Bell, Jason B., McIvor, R. Scott, Hackett, Perry B.
Published 2013

A Broad Range of Dose Optima Achieve High-level, Long-term Gene Expression After Hydrodynamic Delivery of Sleeping Beauty Transposons Using Hyperactive SB100x Transposase

by Podetz-Pedersen, Kelly M, Olson, Erik R, Somia, Nikunj V, Russell, Stephen J, McIvor, R Scott
Published 2016

Conditional gene expression in the mouse using a Sleeping Beauty gene-trap transposon

by Geurts, Aron M, Wilber, Andrew, Carlson, Corey M, Lobitz, Paul D, Clark, Karl J, Hackett, Perry B, McIvor, R Scott, Largaespada, David A
Published 2006

Harnessing a High Cargo-Capacity Transposon for Genetic Applications in Vertebrates

by Balciunas, Darius, Wangensteen, Kirk J, Wilber, Andrew, Bell, Jason, Geurts, Aron, Sivasubbu, Sridhar, Wang, Xin, Hackett, Perry B, Largaespada, David A, McIvor, R. Scott, Ekker, Stephen C
Published 2006

Efficient Non-Viral Integration and Stable Gene Expression in Multipotent Adult Progenitor Cells

by Wilber, Andrew, Ulloa Montoya, Fernando, Hammer, Luke, Moriarity, Branden S., Geurts, Aron M., Largaespada, David A., Verfaillie, Catherine M., McIvor, R. Scott, Lakshmipathy, Uma
Published 2011

Biodistribution of adeno-associated virus serotype 9 (AAV9) vector after intrathecal and intravenous delivery in mouse

by Schuster, Daniel J., Dykstra, Jaclyn A., Riedl, Maureen S., Kitto, Kelley F., Belur, Lalitha R., McIvor, R. Scott, Elde, Robert P., Fairbanks, Carolyn A., Vulchanova, Lucy
Published 2014

Increased Longevity and Metabolic Correction Following Syngeneic Bone Marrow Transplantation in a Murine Model of Mucopolysaccharidosis Type I

by Wolf, Daniel A., Lenander, Andrew W., Nan, Zhenhong, Braunlin, Elizabeth A., Podetz-Pedersen, Kelly M., Whitley, Chester B., Gupta, Pankaj, Low, Walter C., McIvor, R. Scott
Published 2011

Supraspinal gene transfer by intrathecal adeno-associated virus serotype 5

by Schuster, Daniel J., Belur, Lalitha R., Riedl, Maureen S., Schnell, Stephen A., Podetz-Pedersen, Kelly M., Kitto, Kelley F., McIvor, R. Scott, Vulchanova, Lucy, Fairbanks, Carolyn A.
Published 2014

Simple and Efficient Methods for Enrichment and Isolation of Endonuclease Modified Cells

by Moriarity, Branden S., Rahrmann, Eric P., Beckmann, Dominic A., Conboy, Caitlin B., Watson, Adrienne L., Carlson, Daniel F., Olson, Erik R., Hyland, Kendra A., Fahrenkrug, Scott C., McIvor, R. Scott, Largaespada, David A.
Published 2014

An ex vivo Gene Therapy Approach to Treat Muscular Dystrophy Using inducible Pluripotent Stem Cells

by Filareto, Antonio, Parker, Sarah, Darabi, Radbod, Borges, Luciene, Iacovino, Michelina, Schaaf, Tory, Mayerhofer, Timothy, Chamberlain, Jeffrey S, Ervasti, James M., McIvor, R. Scott, Kyba, Michael, Perlingeiro, Rita C.R.
Published 2013

Pax3-induced expansion enables the genetic correction of dystrophic satellite cells

by Filareto, Antonio, Rinaldi, Fabrizio, Arpke, Robert W., Darabi, Radbod, Belanto, Joseph J., Toso, Erik A., Miller, Auston Z., Ervasti, James M., McIvor, R. Scott, Kyba, Michael, Perlingeiro, Rita CR
Published 2015