Development of Lentiviral Vectors Simultaneously Expressing Multiple siRNAs Against CCR5, vif and tat/rev Genes for an HIV-1 Gene Therapy Approach

by Spanevello, Francesca, Calistri, Arianna, Del Vecchio, Claudia, Mantelli, Barbara, Frasson, Chiara, Basso, Giuseppe, Palù, Giorgio, Cavazzana, Marina, Parolin, Cristina
Published 2016

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the βA(T87Q)-Globin Gene

by Negre, Olivier, Eggimann, Anne-Virginie, Beuzard, Yves, Ribeil, Jean-Antoine, Bourget, Philippe, Borwornpinyo, Suparerk, Hongeng, Suradej, Hacein-Bey, Salima, Cavazzana, Marina, Leboulch, Philippe, Payen, Emmanuel
Published 2016

Comparing genotoxic signatures in cord blood cells from neonates exposed in utero to zidovudine or tenofovir

by Vivanti, Alexandre, Soheili, Tayebeh S., Cuccuini, Wendy, Luce, Sonia, Mandelbrot, Laurent, Lechenadec, Jerome, Cordier, Anne-Gael, Azria, Elie, Soulier, Jean, Cavazzana, Marina, Blanche, Stéphane, André-Schmutz, Isabelle
Published 2015

Preclinical Evaluation of Efficacy and Safety of an Improved Lentiviral Vector for the Treatment of β-Thalassemia and Sickle Cell Disease

by Negre, Olivier, Bartholomae, Cynthia, Beuzard, Yves, Cavazzana, Marina, Christiansen, Lauryn, Courne, Céline, Deichmann, Annette, Denaro, Maria, de Dreuzy, Edouard, Finer, Mitchell, Fronza, Raffaele, Gillet-Legrand, Béatrix, Joubert, Christophe, Kutner, Robert, Leboulch, Philippe, Maouche, Leïla, Paulard, Anaïs, Pierciey, Francis J., Rothe, Michael, Ryu, Byoung, Schmidt, Manfred, von Kalle, Christof, Payen, Emmanuel, Veres, Gabor
Published 2015

An inherited immunoglobulin class-switch recombination deficiency associated with a defect in the INO80 chromatin remodeling complex

by Kracker, Sven, Di Virgilio, Michela, Schwartzentruber, Jeremy, Cuenin, Cyrille, Forveille, Monique, Deau, Marie-Céline, McBride, Kevin M., Majewski, Jacek, Gazumyan, Anna, Seneviratne, Suranjith, Grimbacher, Bodo, Kutukculer, Necil, Herceg, Zdenko, Cavazzana, Marina, Jabado, Nada, Nussenzweig, Michel C., Fischer, Alain, Durandy, Anne
Published 2015