Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial

The HERBY trial was a phase II open-label, randomized, multicenter trial evaluating bevacizumab (BEV) in addition to temozolomide/radiotherapy in patients with newly diagnosed non-brainstem high-grade glioma (HGG) between the ages of 3 and 18 years. We carried out comprehensive molecular analysis in...

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Main Authors: Mackay, Alan, Burford, Anna, Molinari, Valeria, Jones, David T.W., Izquierdo, Elisa, Brouwer-Visser, Jurriaan, Giangaspero, Felice, Haberler, Christine, Pietsch, Torsten, Jacques, Thomas S., Figarella-Branger, Dominique, Rodriguez, Daniel, Morgan, Paul S., Raman, Pichai, Waanders, Angela J., Resnick, Adam C., Massimino, Maura, Garrè, Maria Luisa, Smith, Helen, Capper, David, Pfister, Stefan M., Würdinger, Thomas, Tam, Rachel, Garcia, Josep, Thakur, Meghna Das, Vassal, Gilles, Grill, Jacques, Jaspan, Tim, Varlet, Pascale, Jones, Chris
Format: Article
Language:English
Published: Elsevier 2018
Subjects:
Online Access:https://eprints.nottingham.ac.uk/51975/
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author Mackay, Alan
Burford, Anna
Molinari, Valeria
Jones, David T.W.
Izquierdo, Elisa
Brouwer-Visser, Jurriaan
Giangaspero, Felice
Haberler, Christine
Pietsch, Torsten
Jacques, Thomas S.
Figarella-Branger, Dominique
Rodriguez, Daniel
Morgan, Paul S.
Raman, Pichai
Waanders, Angela J.
Resnick, Adam C.
Massimino, Maura
Garrè, Maria Luisa
Smith, Helen
Capper, David
Pfister, Stefan M.
Würdinger, Thomas
Tam, Rachel
Garcia, Josep
Thakur, Meghna Das
Vassal, Gilles
Grill, Jacques
Jaspan, Tim
Varlet, Pascale
Jones, Chris
author_facet Mackay, Alan
Burford, Anna
Molinari, Valeria
Jones, David T.W.
Izquierdo, Elisa
Brouwer-Visser, Jurriaan
Giangaspero, Felice
Haberler, Christine
Pietsch, Torsten
Jacques, Thomas S.
Figarella-Branger, Dominique
Rodriguez, Daniel
Morgan, Paul S.
Raman, Pichai
Waanders, Angela J.
Resnick, Adam C.
Massimino, Maura
Garrè, Maria Luisa
Smith, Helen
Capper, David
Pfister, Stefan M.
Würdinger, Thomas
Tam, Rachel
Garcia, Josep
Thakur, Meghna Das
Vassal, Gilles
Grill, Jacques
Jaspan, Tim
Varlet, Pascale
Jones, Chris
author_sort Mackay, Alan
building Nottingham Research Data Repository
collection Online Access
description The HERBY trial was a phase II open-label, randomized, multicenter trial evaluating bevacizumab (BEV) in addition to temozolomide/radiotherapy in patients with newly diagnosed non-brainstem high-grade glioma (HGG) between the ages of 3 and 18 years. We carried out comprehensive molecular analysis integrated with pathology, radiology, and immune profiling. In post-hoc subgroup analysis, hypermutator tumors (mismatch repair deficiency and somatic POLE/POLD1 mutations) and those biologically resembling pleomorphic xanthoastrocytoma ([PXA]-like, driven by BRAF_V600E or NF1 mutation) had significantly more CD8+ tumor-infiltrating lymphocytes, and longer survival with the addition of BEV. Histone H3 subgroups (hemispheric G34R/V and midline K27M) had a worse outcome and were immune cold. Future clinical trials will need to take into account the diversity represented by the term ‘‘HGG’’ in the pediatric population.
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spelling nottingham-519752018-05-24T00:10:57Z https://eprints.nottingham.ac.uk/51975/ Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial Mackay, Alan Burford, Anna Molinari, Valeria Jones, David T.W. Izquierdo, Elisa Brouwer-Visser, Jurriaan Giangaspero, Felice Haberler, Christine Pietsch, Torsten Jacques, Thomas S. Figarella-Branger, Dominique Rodriguez, Daniel Morgan, Paul S. Raman, Pichai Waanders, Angela J. Resnick, Adam C. Massimino, Maura Garrè, Maria Luisa Smith, Helen Capper, David Pfister, Stefan M. Würdinger, Thomas Tam, Rachel Garcia, Josep Thakur, Meghna Das Vassal, Gilles Grill, Jacques Jaspan, Tim Varlet, Pascale Jones, Chris The HERBY trial was a phase II open-label, randomized, multicenter trial evaluating bevacizumab (BEV) in addition to temozolomide/radiotherapy in patients with newly diagnosed non-brainstem high-grade glioma (HGG) between the ages of 3 and 18 years. We carried out comprehensive molecular analysis integrated with pathology, radiology, and immune profiling. In post-hoc subgroup analysis, hypermutator tumors (mismatch repair deficiency and somatic POLE/POLD1 mutations) and those biologically resembling pleomorphic xanthoastrocytoma ([PXA]-like, driven by BRAF_V600E or NF1 mutation) had significantly more CD8+ tumor-infiltrating lymphocytes, and longer survival with the addition of BEV. Histone H3 subgroups (hemispheric G34R/V and midline K27M) had a worse outcome and were immune cold. Future clinical trials will need to take into account the diversity represented by the term ‘‘HGG’’ in the pediatric population. Elsevier 2018-05-14 Article PeerReviewed application/pdf en cc_by https://eprints.nottingham.ac.uk/51975/1/mmc7.pdf Mackay, Alan, Burford, Anna, Molinari, Valeria, Jones, David T.W., Izquierdo, Elisa, Brouwer-Visser, Jurriaan, Giangaspero, Felice, Haberler, Christine, Pietsch, Torsten, Jacques, Thomas S., Figarella-Branger, Dominique, Rodriguez, Daniel, Morgan, Paul S., Raman, Pichai, Waanders, Angela J., Resnick, Adam C., Massimino, Maura, Garrè, Maria Luisa, Smith, Helen, Capper, David, Pfister, Stefan M., Würdinger, Thomas, Tam, Rachel, Garcia, Josep, Thakur, Meghna Das, Vassal, Gilles, Grill, Jacques, Jaspan, Tim, Varlet, Pascale and Jones, Chris (2018) Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial. Cancer Cell, 33 (5). 829-842.e5. ISSN 1878-3686 Immune; CD8; MAPK; Hypermutator; H3F3A; Pediatric high-grade glioma https://www.sciencedirect.com/science/article/pii/S1535610818301752?via%3Dihub doi:10.1016/j.ccell.2018.04.004 doi:10.1016/j.ccell.2018.04.004
spellingShingle Immune; CD8; MAPK; Hypermutator; H3F3A; Pediatric high-grade glioma
Mackay, Alan
Burford, Anna
Molinari, Valeria
Jones, David T.W.
Izquierdo, Elisa
Brouwer-Visser, Jurriaan
Giangaspero, Felice
Haberler, Christine
Pietsch, Torsten
Jacques, Thomas S.
Figarella-Branger, Dominique
Rodriguez, Daniel
Morgan, Paul S.
Raman, Pichai
Waanders, Angela J.
Resnick, Adam C.
Massimino, Maura
Garrè, Maria Luisa
Smith, Helen
Capper, David
Pfister, Stefan M.
Würdinger, Thomas
Tam, Rachel
Garcia, Josep
Thakur, Meghna Das
Vassal, Gilles
Grill, Jacques
Jaspan, Tim
Varlet, Pascale
Jones, Chris
Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial
title Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial
title_full Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial
title_fullStr Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial
title_full_unstemmed Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial
title_short Molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the HERBY phase II randomized trial
title_sort molecular, pathological, radiological, and immune profiling of non-brainstem pediatric high-grade glioma from the herby phase ii randomized trial
topic Immune; CD8; MAPK; Hypermutator; H3F3A; Pediatric high-grade glioma
url https://eprints.nottingham.ac.uk/51975/
https://eprints.nottingham.ac.uk/51975/
https://eprints.nottingham.ac.uk/51975/