The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury

Background & Aims: In vertebrates, canonical Hedgehog (Hh) pathway activation requires Smoothened (SMO) translocation to the primary cilium (Pc), followed by a GLI-mediated transcriptional response. In addition, a similar gene regulation occurs in response to growth factors/cytokines, although i...

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Main Authors: Grzelak, C., Martelotto, L., Sigglekow, N., Patkunanathan, B., Ajami, K., Calabro, S., Dwyer, Benjamin, Tirnitz-Parker, Janina, Watkins, D., Warner, F., Shackel, N., McCaughan, G.
Format: Journal Article
Published: Elsevier BV 2014
Online Access:http://hdl.handle.net/20.500.11937/42482
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author Grzelak, C.
Martelotto, L.
Sigglekow, N.
Patkunanathan, B.
Ajami, K.
Calabro, S.
Dwyer, Benjamin
Tirnitz-Parker, Janina
Watkins, D.
Warner, F.
Shackel, N.
McCaughan, G.
author_facet Grzelak, C.
Martelotto, L.
Sigglekow, N.
Patkunanathan, B.
Ajami, K.
Calabro, S.
Dwyer, Benjamin
Tirnitz-Parker, Janina
Watkins, D.
Warner, F.
Shackel, N.
McCaughan, G.
author_sort Grzelak, C.
building Curtin Institutional Repository
collection Online Access
description Background & Aims: In vertebrates, canonical Hedgehog (Hh) pathway activation requires Smoothened (SMO) translocation to the primary cilium (Pc), followed by a GLI-mediated transcriptional response. In addition, a similar gene regulation occurs in response to growth factors/cytokines, although independently of SMO signalling. The Hh pathway plays a critical role in liver fibrosis/regeneration; however, the mechanism of activation in chronic liver injury is poorly understood. This study aimed to characterise Hh pathway activation upon thioacetamide (TAA)- induced chronic liver injury in vivo by defining Hh-responsive cells, namely cells harbouring Pc and Pc-localised SMO. Methods: C57BL/6 mice (wild-type or Ptc1+/_) were TAA-treated. Liver injury and Hh ligand/pathway mRNA and protein expression were assessed in vivo. SMO/GLI manipulation and SMO dependent/ independent activation of GLI-mediated transcriptional response in Pc-positive (Pc+) cells were studied in vitro. Results: In vivo, Hh activation was progressively induced following TAA. At the epithelial-mesenchymal interface, injured hepatocytes produced Hh ligands. Progenitors, myofibroblasts, leukocytes and hepatocytes were GLI2+. Pc+ cells increased following TAA, but only EpCAM+/GLI2+ progenitors were Pc+/SMO+. In vitro, SMO knockdown/hGli3-R overexpression reduced proliferation/viability in Pc+ progenitors, whilst increased proliferation occurred with hGli1 overexpression. HGF induced GLI transcriptional activity independently of Pc/SMO. Ptc1+/_ mice exhibited increased progenitor, myofibroblast and fibrosis responses. Conclusions: In chronic liver injury, Pc+ progenitors receive Hh ligand signals and process it through Pc/SMO-dependent activation of GLI-mediated transcriptional response. Pc/SMO-independent GLI activation likely occurs in Pc_/GLI2+ cells. Increased fibrosis in Hh gain-of-function mice likely occurs by primary progenitor expansion/proliferation and secondary fibrotic myofibroblast expansion, in close contact with progenitors.
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publishDate 2014
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spelling curtin-20.500.11937-424822019-02-19T05:35:17Z The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury Grzelak, C. Martelotto, L. Sigglekow, N. Patkunanathan, B. Ajami, K. Calabro, S. Dwyer, Benjamin Tirnitz-Parker, Janina Watkins, D. Warner, F. Shackel, N. McCaughan, G. Background & Aims: In vertebrates, canonical Hedgehog (Hh) pathway activation requires Smoothened (SMO) translocation to the primary cilium (Pc), followed by a GLI-mediated transcriptional response. In addition, a similar gene regulation occurs in response to growth factors/cytokines, although independently of SMO signalling. The Hh pathway plays a critical role in liver fibrosis/regeneration; however, the mechanism of activation in chronic liver injury is poorly understood. This study aimed to characterise Hh pathway activation upon thioacetamide (TAA)- induced chronic liver injury in vivo by defining Hh-responsive cells, namely cells harbouring Pc and Pc-localised SMO. Methods: C57BL/6 mice (wild-type or Ptc1+/_) were TAA-treated. Liver injury and Hh ligand/pathway mRNA and protein expression were assessed in vivo. SMO/GLI manipulation and SMO dependent/ independent activation of GLI-mediated transcriptional response in Pc-positive (Pc+) cells were studied in vitro. Results: In vivo, Hh activation was progressively induced following TAA. At the epithelial-mesenchymal interface, injured hepatocytes produced Hh ligands. Progenitors, myofibroblasts, leukocytes and hepatocytes were GLI2+. Pc+ cells increased following TAA, but only EpCAM+/GLI2+ progenitors were Pc+/SMO+. In vitro, SMO knockdown/hGli3-R overexpression reduced proliferation/viability in Pc+ progenitors, whilst increased proliferation occurred with hGli1 overexpression. HGF induced GLI transcriptional activity independently of Pc/SMO. Ptc1+/_ mice exhibited increased progenitor, myofibroblast and fibrosis responses. Conclusions: In chronic liver injury, Pc+ progenitors receive Hh ligand signals and process it through Pc/SMO-dependent activation of GLI-mediated transcriptional response. Pc/SMO-independent GLI activation likely occurs in Pc_/GLI2+ cells. Increased fibrosis in Hh gain-of-function mice likely occurs by primary progenitor expansion/proliferation and secondary fibrotic myofibroblast expansion, in close contact with progenitors. 2014 Journal Article http://hdl.handle.net/20.500.11937/42482 10.1016/j.jhep.2013.08.012 Elsevier BV fulltext
spellingShingle Grzelak, C.
Martelotto, L.
Sigglekow, N.
Patkunanathan, B.
Ajami, K.
Calabro, S.
Dwyer, Benjamin
Tirnitz-Parker, Janina
Watkins, D.
Warner, F.
Shackel, N.
McCaughan, G.
The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury
title The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury
title_full The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury
title_fullStr The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury
title_full_unstemmed The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury
title_short The intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury
title_sort intrahepatic signalling niche of hedgehog is defined by primary cilia positive cells during chronic liver injury
url http://hdl.handle.net/20.500.11937/42482