Enzyme Replacement in Gaucher Disease
The development of enzyme replacement therapy for Gaucher disease was a triumph of translational medicine. What were the key steps in its development? What are the controversies surrounding its use?
| Main Author: | |
|---|---|
| Format: | Online |
| Language: | English |
| Published: |
Public Library of Science
2004
|
| Online Access: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC529421/ |