Gene therapy for metabolic diseases
Gene therapy has recently shown great promise as an effective treatment for a number of metabolic diseases caused by genetic defects in both animal models and human clinical trials. Most of the current success has been achieved using a viral mediated gene addition approach, but gene-editing technolo...
| Main Authors: | , |
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| Format: | Online |
| Language: | English |
| Published: |
IOS Press
2016
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| Online Access: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5108627/ |