Adeno-Associated Virus-Based Gene Therapy for CNS Diseases
Gene therapy is at the cusp of a revolution for treating a large spectrum of CNS disorders by providing a durable therapeutic protein via a single administration. Adeno-associated virus (AAV)-mediated gene transfer is of particular interest as a therapeutic tool because of its safety profile and eff...
| Main Authors: | , , , , |
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| Format: | Online |
| Language: | English |
| Published: |
Mary Ann Liebert, Inc.
2016
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| Online Access: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4960479/ |