Impact of Imiglucerase Supply Shortage on Clinical and Laboratory Parameters in Norrbottnian Patients with Gaucher Disease Type 3

A viral contamination of the production plant producing imiglucerase (Cerezyme™) resulted in an unpredicted worldwide shortage of global supplies during 2009–2010. The aim of the study was to describe the effects of dose reduction of enzyme replacement therapy (ERT) in adults with Norrbottnian form...

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Bibliographic Details
Main Authors: Machaczka, Maciej, Kämpe Björkvall, Cecilia, Wieremiejczyk, Joanna, Paucar Arce, Martin, Myhr-Eriksson, Kristina, Klimkowska, Monika, Hägglund, Hans, Svenningsson, Per
Format: Online
Language:English
Published: Springer Basel 2014
Online Access:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4289531/