Therapeutic strategies based on modified U1 snRNAs and chaperones for Sanfilippo C splicing mutations

Therapeutic strategies based on modified U1 snRNAs and chaperones for Sanfilippo C splicing mutations

Bibliographic Details
Main Authors:	Matos, Liliana, Canals, Isaac, Dridi, Larbi, Choi, Yoo, Prata, Maria João, Jordan, Peter, Desviat, Lourdes R, Pérez, Belén, Pshezhetsky, Alexey V, Grinberg, Daniel, Alves, Sandra, Vilageliu, Lluïsa
Format:	Online
Language:	English
Published:	BioMed Central 2014
Online Access:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4279800/

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