The Liver as a Target Organ for Gene Therapy: State of the Art, Challenges, and Future Perspectives
The liver is a target for gene therapy of inborn errors of metabolism, of hemophilia, and of acquired diseases such as liver cancer and hepatitis. The ideal gene transfer strategy should deliver the transgene DNA to parenchymal liver cells with accuracy and precision in the absence of side effects....
| Main Authors: | , , , |
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| Format: | Online |
| Language: | English |
| Published: |
MDPI
2012
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| Online Access: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3816670/ |