Splicing therapy for neuromuscular disease☆

by Douglas, Andrew G.L., Wood, Matthew J.A.
Published 2013

The acute inflammatory response to intranigral α-synuclein differs significantly from intranigral lipopolysaccharide and is exacerbated by peripheral inflammation

by Couch, Yvonne, Alvarez-Erviti, Lydia, Sibson, Nicola R, Wood, Matthew JA, Anthony, Daniel C
Published 2011

Peptide-mediated Cell and In Vivo Delivery of Antisense Oligonucleotides and siRNA

by Järver, Peter, Coursindel, Thibault, Andaloussi, Samir EL, Godfrey, Caroline, Wood, Matthew JA, Gait, Michael J
Published 2012

Small RNA-Mediated Epigenetic Myostatin Silencing

by Roberts, Thomas C, Andaloussi, Samir EL, Morris, Kevin V, McClorey, Graham, Wood, Matthew JA
Published 2012

Natural Antisense Makes Sense for Gene-specific Activation in Brain

by Varela, Miguel A, Roberts, Thomas C, Andaloussi, Samir EL, Wood, Matthew JA
Published 2012

Lysosomal dysfunction increases exosome-mediated alpha-synuclein release and transmission

by Alvarez-Erviti, Lydia, Seow, Yiqi, Schapira, Anthony H., Gardiner, Chris, Sargent, Ian L., Wood, Matthew J.A., Cooper, J. Mark
Published 2011

mRNA and microRNA transcriptomics analyses in a murine model of dystrophin loss and therapeutic restoration

by Roberts, Thomas C., Blomberg, K. Emelie M., Smith, C.I. Edvard, EL Andaloussi, Samir, Wood, Matthew J.A.
Published 2015

Bi-specific splice-switching PMO oligonucleotides conjugated via a single peptide active in a mouse model of Duchenne muscular dystrophy

by Shabanpoor, Fazel, McClorey, Graham, Saleh, Amer F., Järver, Peter, Wood, Matthew J.A., Gait, Michael J.
Published 2015

Expression Analysis in Multiple Muscle Groups and Serum Reveals Complexity in the MicroRNA Transcriptome of the mdx Mouse with Implications for Therapy

by Roberts, Thomas C, Blomberg, K Emelie M, McClorey, Graham, Andaloussi, Samir EL, Godfrey, Caroline, Betts, Corinne, Coursindel, Thibault, Gait, Michael J, Edvard Smith, CI, Wood, Matthew JA
Published 2012

Pip6-PMO, A New Generation of Peptide-oligonucleotide Conjugates With Improved Cardiac Exon Skipping Activity for DMD Treatment

by Betts, Corinne, Saleh, Amer F, Arzumanov, Andrey A, Hammond, Suzan M, Godfrey, Caroline, Coursindel, Thibault, Gait, Michael J, Wood, Matthew JA
Published 2012

Dual Myostatin and Dystrophin Exon Skipping by Morpholino Nucleic Acid Oligomers Conjugated to a Cell-penetrating Peptide Is a Promising Therapeutic Strategy for the Treatment of D...

by Malerba, Alberto, Kang, Jagjeet K, McClorey, Graham, Saleh, Amer F, Popplewell, Linda, Gait, Michael J, Wood, Matthew JA, Dickson, George
Published 2012

Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency

by Yin, HaiFang, Boisguerin, Prisca, Moulton, Hong M, Betts, Corinne, Seow, Yiqi, Boutilier, Jordan, Wang, Qingsong, Walsh, Anthony, Lebleu, Bernard, Wood, Matthew JA
Published 2013

Extracellular microRNAs are dynamic non-vesicular biomarkers of muscle turnover

by Roberts, Thomas C., Godfrey, Caroline, McClorey, Graham, Vader, Pieter, Briggs, Deborah, Gardiner, Chris, Aoki, Yoshitsugu, Sargent, Ian, Morgan, Jennifer E., Wood, Matthew J.A.
Published 2013

Cells release subpopulations of exosomes with distinct molecular and biological properties

by Willms, Eduard, Johansson, Henrik J., Mäger, Imre, Lee, Yi, Blomberg, K. Emelie M., Sadik, Mariam, Alaarg, Amr, Smith, C.I. Edvard, Lehtiö, Janne, EL Andaloussi, Samir, Wood, Matthew J.A., Vader, Pieter
Published 2016

Multi-level omics analysis in a murine model of dystrophin loss and therapeutic restoration

by Roberts, Thomas C., Johansson, Henrik J., McClorey, Graham, Godfrey, Caroline, Blomberg, K. Emelie M., Coursindel, Thibault, Gait, Michael J., Smith, C.I. Edvard, Lehtiö, Janne, EL Andaloussi, Samir, Wood, Matthew J.A.
Published 2015

Peptide Nanoparticle Delivery of Charge-Neutral Splice-Switching Morpholino Oligonucleotides

by Järver, Peter, Zaghloul, Eman M., Arzumanov, Andrey A., Saleh, Amer F., McClorey, Graham, Hammond, Suzan M., Hällbrink, Mattias, Langel, Ülo, Smith, C.I. Edvard, Wood, Matthew J.A., Gait, Michael J., EL Andaloussi, Samir
Published 2015

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-...

by Cirak, Sebahattin, Arechavala-Gomeza, Virginia, Guglieri, Michela, Feng, Lucy, Torelli, Silvia, Anthony, Karen, Abbs, Stephen, Garralda, Maria Elena, Bourke, John, Wells, Dominic J, Dickson, George, Wood, Matthew JA, Wilton, Steve D, Straub, Volker, Kole, Ryszard, Shrewsbury, Stephen B, Sewry, Caroline, Morgan, Jennifer E, Bushby, Kate, Muntoni, Francesco
Published 2011

The CRTC1-SIK1 Pathway Regulates Entrainment of the Circadian Clock

by Jagannath, Aarti, Butler, Rachel, Godinho, Sofia I.H., Couch, Yvonne, Brown, Laurence A., Vasudevan, Sridhar R., Flanagan, Kevin C., Anthony, Daniel, Churchill, Grant C., Wood, Matthew J.A., Steiner, Guido, Ebeling, Martin, Hossbach, Markus, Wettstein, Joseph G., Duffield, Giles E., Gatti, Silvia, Hankins, Mark W., Foster, Russell G., Peirson, Stuart N.
Published 2013

Serum proteomic profiling reveals fragments of MYOM3 as potential biomarkers for monitoring the outcome of therapeutic interventions in muscular dystrophies

by Rouillon, Jérémy, Poupiot, Jérôme, Zocevic, Aleksandar, Amor, Fatima, Léger, Thibaut, Garcia, Camille, Camadro, Jean-Michel, Wong, Brenda, Pinilla, Robin, Cosette, Jérémie, Coenen-Stass, Anna M.L., Mcclorey, Graham, Roberts, Thomas C., Wood, Matthew J.A., Servais, Laurent, Udd, Bjarne, Voit, Thomas, Richard, Isabelle, Svinartchouk, Fedor
Published 2015

Lipid-based Transfection Reagents Exhibit Cryo-induced Increase in Transfection Efficiency

by Sork, Helena, Nordin, Joel Z, Turunen, Janne J, Wiklander, Oscar PB, Bestas, Burcu, Zaghloul, Eman M, Margus, Helerin, Padari, Kärt, Duru, Adil D, Corso, Giulia, Bost, Jeremy, Vader, Pieter, Pooga, Margus, Smith, CI Edvard, Wood, Matthew JA, Schiffelers, Raymond M, Hällbrink, Mattias, Andaloussi, Samir EL
Published 2016