Antisense suppression of donor splice site mutations in the dystrophin gene transcript

by Fletcher, Sue, Meloni, Penny L, Johnsen, Russell D, Wong, Brenda L, Muntoni, Francesco, Wilton, Stephen D
Published 2013

Targeted Exon Skipping to Address “Leaky” Mutations in the Dystrophin Gene

by Fletcher, Sue, Adkin, Carl F., Meloni, Penny, Wong, Brenda, Muntoni, Francesco, Kole, Ryszard, Fragall, Clayton, Greer, Kane, Johnsen, Russell, Wilton, Steve D.
Published 2012