IGF-I instructs multipotent adult neural progenitor cells to become oligodendrocytes

by Hsieh, Jenny, Aimone, James B., Kaspar, Brian K., Kuwabara, Tomoko, Nakashima, Kinichi, Gage, Fred H.
Published 2004

AAV1.NT-3 Gene Therapy for Charcot–Marie–Tooth Neuropathy

by Sahenk, Zarife, Galloway, Gloria, Clark, Kelly Reed, Malik, Vinod, Rodino-Klapac, Louise R, Kaspar, Brian K., Chen, Lei, Braganza, Cilwyn, Montgomery, Chrystal, Mendell, Jerry R
Published 2014

Gene therapy rescues disease phenotype in a spinal muscular atrophy with respiratory distress type 1 (SMARD1) mouse model

by Nizzardo, Monica, Simone, Chiara, Rizzo, Federica, Salani, Sabrina, Dametti, Sara, Rinchetti, Paola, Del Bo, Roberto, Foust, Kevin, Kaspar, Brian K., Bresolin, Nereo, Comi, Giacomo P., Corti, Stefania
Published 2015

Electrophysiological biomarkers in spinal muscular atrophy: proof of concept

by David Arnold, W, Porensky, Paul N, McGovern, Vicki L, Iyer, Chitra C, Duque, Sandra, Li, Xiaobai, Meyer, Kathrin, Schmelzer, Leah, Kaspar, Brian K, Kolb, Stephen J, Kissel, John T, Burghes, Arthur H M
Published 2014

MHC class I protects motor neurons from astrocyte-induced toxicity in amyotrophic lateral sclerosis (ALS)

by Song, SungWon, Miranda, Carlos J., Braun, Lyndsey, Meyer, Kathrin, Frakes, Ashley E., Ferraiuolo, Laura, Likhite, Shibi, Bevan, Adam K., Foust, Kevin D., McConnell, Michael J., Walker, Christopher M., Kaspar, Brian K.
Published 2016

Potent spinal parenchymal AAV9-mediated gene delivery by subpial injection in adult rats and pigs

by Miyanohara, Atsushi, Kamizato, Kota, Juhas, Stefan, Juhasova, Jana, Navarro, Michael, Marsala, Silvia, Lukacova, Nada, Hruska-Plochan, Marian, Curtis, Erik, Gabel, Brandon, Ciacci, Joseph, Ahrens, Eric T, Kaspar, Brian K, Cleveland, Don, Marsala, Martin
Published 2016

Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders

by Bevan, Adam K, Duque, Sandra, Foust, Kevin D, Morales, Pablo R, Braun, Lyndsey, Schmelzer, Leah, Chan, Curtis M, McCrate, Mary, Chicoine, Louis G, Coley, Brian D, Porensky, Paul N, Kolb, Stephen J, Mendell, Jerry R, Burghes, Arthur HM, Kaspar, Brian K
Published 2011

Astrocytes from Familial and Sporadic ALS Patients are Toxic to Motor Neurons

by Haidet-Phillips, Amanda M., Hester, Mark E., Miranda, Carlos J., Meyer, Kathrin, Braun, Lyndsey, Frakes, Ashley, Song, SungWon, Likhite, Shibi, Murtha, Matthew J., Foust, Kevin D., Rao, Meghan, Eagle, Amy, Kammesheidt, Anja, Christensen, Ashley, Mendell, Jerry R., Burghes, Arthur H.M., Kaspar, Brian K.
Published 2011

The C9orf72 protein interacts with Rab1a and the ULK1 complex to regulate initiation of autophagy

by Webster, Christopher P, Smith, Emma F, Bauer, Claudia S, Moller, Annekathrin, Hautbergue, Guillaume M, Ferraiuolo, Laura, Myszczynska, Monika A, Higginbottom, Adrian, Walsh, Matthew J, Whitworth, Alexander J, Kaspar, Brian K, Meyer, Kathrin, Shaw, Pamela J, Grierson, Andrew J, De Vos, Kurt J
Published 2016

Gene delivery to the spinal cord using MRI-guided focused ultrasound

by Weber-Adrian, Danielle, Thévenot, Emmanuel, O'Reilly, Meaghan A., Oakden, Wendy, Akens, Margarete K., Ellens, Nicholas, Markham-Coultes, Kelly, Burgess, Alison, Finkelstein, Joel, Yee, Albert J.M., Whyne, Cari M., Foust, Kevin D., Kaspar, Brian K., Stanisz, Greg J., Chopra, Rajiv, Hynynen, Kullervo, Aubert, Isabelle
Published 2015