Toward a gene therapy for neurological and somatic MPSIIIA

by Haurigot, Virginia, Bosch, Fatima
Published 2013

Long-Term Retinal PEDF Overexpression Prevents Neovascularization in a Murine Adult Model of Retinopathy

by Haurigot, Virginia, Villacampa, Pilar, Ribera, Albert, Bosch, Assumpcio, Ramos, David, Ruberte, Jesus, Bosch, Fatima
Published 2012

Treatment of Diabetes and Long-Term Survival After Insulin and Glucokinase Gene Therapy

by Callejas, David, Mann, Christopher J., Ayuso, Eduard, Lage, Ricardo, Grifoll, Iris, Roca, Carles, Andaluz, Anna, Ruiz-de Gopegui, Rafael, Montané, Joel, Muñoz, Sergio, Ferre, Tura, Haurigot, Virginia, Zhou, Shangzhen, Ruberte, Jesús, Mingozzi, Federico, High, Katherine A., Garcia, Felix, Bosch, Fatima
Published 2013

Modulation of CD8+ T cell responses to AAV vectors with IgG-derived MHC class II epitopes

by Hui, Daniel J, Basner-Tschakarjan, Etiena, Chen, Yifeng, Davidson, Robert J, Buchlis, George, Yazicioglu, Mustafa, Pien, Gary C, Finn, Jonathan D, Haurigot, Virginia, Tai, Alex, Scott, David W, Cousens, Leslie P, Zhou, Shangzhen, De Groot, Anne S, Mingozzi, Federico
Published 2013

Progressive neurologic and somatic disease in a novel mouse model of human mucopolysaccharidosis type IIIC

by Marcó, Sara, Pujol, Anna, Roca, Carles, Motas, Sandra, Ribera, Albert, Garcia, Miguel, Molas, Maria, Villacampa, Pilar, Melia, Cristian S., Sánchez, Víctor, Sánchez, Xavier, Bertolin, Joan, Ruberte, Jesús, Haurigot, Virginia, Bosch, Fatima
Published 2016

In vivo genome editing restores hemostasis in a mouse model of hemophilia

by Li, Hojun, Haurigot, Virginia, Doyon, Yannick, Li, Tianjian, Wong, Sunnie Y., Bhagwat, Anand S., Malani, Nirav, Anguela, Xavier M., Sharma, Rajiv, Ivanciu, Lacramiora, Murphy, Samuel L., Finn, Jonathan D., Khazi, Fayaz R., Zhou, Shangzhen, Paschon, David E., Rebar, Edward J., Bushman, Frederic D., Gregory, Philip D., Holmes, Michael C., High, Katherine A.
Published 2011