Repair of Mybpc3 mRNA by 5′-trans-splicing in a Mouse Model of Hypertrophic Cardiomyopathy

by Mearini, Giulia, Stimpel, Doreen, Krämer, Elisabeth, Geertz, Birgit, Braren, Ingke, Gedicke-Hornung, Christina, Précigout, Guillaume, Müller, Oliver J, Katus, Hugo A, Eschenhagen, Thomas, Voit, Thomas, Garcia, Luis, Lorain, Stéphanie, Carrier, Lucie
Published 2013

Rescue of cardiomyopathy through U7snRNA-mediated exon skipping in Mybpc3-targeted knock-in mice

by Gedicke-Hornung, Christina, Behrens-Gawlik, Verena, Reischmann, Silke, Geertz, Birgit, Stimpel, Doreen, Weinberger, Florian, Schlossarek, Saskia, Précigout, Guillaume, Braren, Ingke, Eschenhagen, Thomas, Mearini, Giulia, Lorain, Stéphanie, Voit, Thomas, Dreyfus, Patrick A, Garcia, Luis, Carrier, Lucie
Published 2013