A Double-Blinded, Randomized, Placebo-Controlled Trial to Evaluate Efficacy, Safety, and Tolerability of Single Doses of Tirasemtiv in Patients with Acetylcholine Receptor-Binding...

by Sanders, Donald B., Rosenfeld, Jeffrey, Dimachkie, Mazen M., Meng, Lisa, Malik, Fady I.
Published 2015

Long-Term Neurological Outcomes in West Nile Virus–Infected Patients: An Observational Study

by Weatherhead, Jill E., Miller, Vicki E., Garcia, Melissa N., Hasbun, Rodrigo, Salazar, Lucrecia, Dimachkie, Mazen M., Murray, Kristy O.
Published 2015

A Bayesian comparative effectiveness trial in action: developing a platform for multisite study adaptive randomization

by Brown, Alexandra R., Gajewski, Byron J., Aaronson, Lauren S., Mudaranthakam, Dinesh Pal, Hunt, Suzanne L., Berry, Scott M., Quintana, Melanie, Pasnoor, Mamatha, Dimachkie, Mazen M., Jawdat, Omar, Herbelin, Laura, Barohn, Richard J.
Published 2016

Compromised fidelity of B‐cell tolerance checkpoints in AChR and MuSK myasthenia gravis

by Lee, Jae‐Yun, Stathopoulos, Panos, Gupta, Sasha, Bannock, Jason M., Barohn, Richard J., Cotzomi, Elizabeth, Dimachkie, Mazen M., Jacobson, Leslie, Lee, Casey S., Morbach, Henner, Querol, Luis, Shan, Jing‐Li, Vander Heiden, Jason A., Waters, Patrick, Vincent, Angela, Nowak, Richard J., O'Connor, Kevin C.
Published 2016

The effects of an intronic polymorphism in TOMM40 and APOE genotypes in sporadic inclusion body myositis

by Gang, Qiang, Bettencourt, Conceicao, Machado, Pedro M., Fox, Zoe, Brady, Stefen, Healy, Estelle, Parton, Matt, Holton, Janice L., Hilton-Jones, David, Shieh, Perry B., Zanoteli, Edmar, De Paepe, Boel, De Bleecker, Jan, Shaibani, Aziz, Ripolone, Michela, Violano, Raffaella, Moggio, Maurizio, Barohn, Richard J., Dimachkie, Mazen M., Mora, Marina, Mantegazza, Renato, Zanotti, Simona, Hanna, Michael G., Houlden, Henry
Published 2015

Rare variants in SQSTM1 and VCP genes and risk of sporadic inclusion body myositis

by Gang, Qiang, Bettencourt, Conceição, Machado, Pedro M., Brady, Stefen, Holton, Janice L., Pittman, Alan M., Hughes, Deborah, Healy, Estelle, Parton, Matthew, Hilton-Jones, David, Shieh, Perry B., Needham, Merrilee, Liang, Christina, Zanoteli, Edmar, de Camargo, Leonardo Valente, De Paepe, Boel, De Bleecker, Jan, Shaibani, Aziz, Ripolone, Michela, Violano, Raffaella, Moggio, Maurizio, Barohn, Richard J., Dimachkie, Mazen M., Mora, Marina, Mantegazza, Renato, Zanotti, Simona, Singleton, Andrew B., Hanna, Michael G., Houlden, Henry
Published 2016