Hunting for a cure: the therapeutic potential of gene therapy in Duchenne muscular dystrophy

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Hunting for a cure: the therapeutic potential of gene therapy in Duchenne muscular dystrophy

Duchenne muscular dystrophy (DMD) is an incurable disease and the search for a cure is a challenging journey. However, with recent encouraging progress, we are seeing a light at the end of a long tunnel. This review focuses on several main strategies in gene therapy, including truncated dystrophin g...

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Bibliographic Details
Main Authors:	Hashim, Hasnur Zaman, Che Abdullah, Shahrin Tarmizi, Wan Sulaiman, Wan Aliaa, Hoo, Fan Kee, Basri, Hamidon
Format:	Article
Language:	English
Published:	Elsevier 2014
Online Access:	http://psasir.upm.edu.my/id/eprint/37897/ http://psasir.upm.edu.my/id/eprint/37897/1/Hunting%20for%20a%20cure%20the%20therapeutic%20potential%20of%20gene%20therapy%20in%20Duchenne%20muscular%20dystrophy.pdf

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