Licensed medicines, off-label use or evidence based: which is most important?

Medicines are licensed for use in humans by regulatory authorities. The concept of licensing is that it helps ensure that medicines are safe, effective and of an adequate quality for regular use.1 Licensing was introduced due to concerns about safety not to ensure that medicines are effective. It wa...

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Main Authors: Bonati, Maurizio, Jacqz-Aigrain, Evelyne, Choonara, Imti
Format: Article
Published: BMJ Publishing Group 2016
Online Access:https://eprints.nottingham.ac.uk/37180/
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author Bonati, Maurizio
Jacqz-Aigrain, Evelyne
Choonara, Imti
author_facet Bonati, Maurizio
Jacqz-Aigrain, Evelyne
Choonara, Imti
author_sort Bonati, Maurizio
building Nottingham Research Data Repository
collection Online Access
description Medicines are licensed for use in humans by regulatory authorities. The concept of licensing is that it helps ensure that medicines are safe, effective and of an adequate quality for regular use.1 Licensing was introduced due to concerns about safety not to ensure that medicines are effective. It was a response to specific examples of drug toxicity, notably the grey baby syndrome in neonates following the use of the antibiotic chloramphenicol and phocomelia in the developing fetus following ingestion of thalidomide by pregnant women.2 Within the UK, the Medicines Act was passed in 1968. The licensing of medicines is both a control on products of public interest as well as an authorisation to sell for pharmaceutical companies. Pharmaceutical companies are only allowed to promote licensed medicines. Prescribers, however, are free to prescribe the most appropriate medicine for their patient. This should be based on the best available scientific evidence. Medicines can be licensed (authorised) by either national regulatory agencies (national route) or the European Medicines Agency
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institution University of Nottingham Malaysia Campus
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publishDate 2016
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spelling nottingham-371802020-05-04T18:06:41Z https://eprints.nottingham.ac.uk/37180/ Licensed medicines, off-label use or evidence based: which is most important? Bonati, Maurizio Jacqz-Aigrain, Evelyne Choonara, Imti Medicines are licensed for use in humans by regulatory authorities. The concept of licensing is that it helps ensure that medicines are safe, effective and of an adequate quality for regular use.1 Licensing was introduced due to concerns about safety not to ensure that medicines are effective. It was a response to specific examples of drug toxicity, notably the grey baby syndrome in neonates following the use of the antibiotic chloramphenicol and phocomelia in the developing fetus following ingestion of thalidomide by pregnant women.2 Within the UK, the Medicines Act was passed in 1968. The licensing of medicines is both a control on products of public interest as well as an authorisation to sell for pharmaceutical companies. Pharmaceutical companies are only allowed to promote licensed medicines. Prescribers, however, are free to prescribe the most appropriate medicine for their patient. This should be based on the best available scientific evidence. Medicines can be licensed (authorised) by either national regulatory agencies (national route) or the European Medicines Agency BMJ Publishing Group 2016-08-17 Article PeerReviewed Bonati, Maurizio, Jacqz-Aigrain, Evelyne and Choonara, Imti (2016) Licensed medicines, off-label use or evidence based: which is most important? Archives of Disease in Childhood . ISSN 1468-2044 http://adc.bmj.com/content/early/2016/08/17/archdischild-2016-311527.extract doi:10.1136/archdischild-2016-311527 doi:10.1136/archdischild-2016-311527
spellingShingle Bonati, Maurizio
Jacqz-Aigrain, Evelyne
Choonara, Imti
Licensed medicines, off-label use or evidence based: which is most important?
title Licensed medicines, off-label use or evidence based: which is most important?
title_full Licensed medicines, off-label use or evidence based: which is most important?
title_fullStr Licensed medicines, off-label use or evidence based: which is most important?
title_full_unstemmed Licensed medicines, off-label use or evidence based: which is most important?
title_short Licensed medicines, off-label use or evidence based: which is most important?
title_sort licensed medicines, off-label use or evidence based: which is most important?
url https://eprints.nottingham.ac.uk/37180/
https://eprints.nottingham.ac.uk/37180/
https://eprints.nottingham.ac.uk/37180/