Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency

Despite research efforts, cell uptake processes determining siRNA silencing efficiency remain unclear. Here, we examine the relationship between in vitro cell culture models, cellular trafficking and siRNA silencing efficiency to provide a mechanistic insight on siRNA delivery system design. Model s...

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Main Authors: Capel, Victoria, Vllasaliu, Driton, Watts, Peter, Stolnik, Snow
Format: Article
Published: Elsevier 2016
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Online Access:https://eprints.nottingham.ac.uk/35333/
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author Capel, Victoria
Vllasaliu, Driton
Watts, Peter
Stolnik, Snow
author_facet Capel, Victoria
Vllasaliu, Driton
Watts, Peter
Stolnik, Snow
author_sort Capel, Victoria
building Nottingham Research Data Repository
collection Online Access
description Despite research efforts, cell uptake processes determining siRNA silencing efficiency remain unclear. Here, we examine the relationship between in vitro cell culture models, cellular trafficking and siRNA silencing efficiency to provide a mechanistic insight on siRNA delivery system design. Model siRNA-polyplexes, based on chitosan as a ‘classical’ condensing agent, were applied to a panel of lung epithelial cell lines, H1299, A549 and Calu-3 and cell internalization levels, trafficking pathways and gene silencing assessed on exposure to pharmacological inhibitors. The data reveal striking differences in the internalization behaviour and gene silencing efficiency in the tested cell lines, despite their common lung epithelial origins. The model system’s silencing was lower where clathrin internalization pathway predominated in Calu-3, relative to silencing in H1299 cells where a non-clathrin internalization appears dominant. Increased silencing on endosomal disruption was apparent in Calu-3 cells, but absent when cellular internalization was not predominantly clathrin-mediated in A549 cells. This highlights that identifying cell trafficking pathways before incorporation of functional components to siRNA delivery systems (e.g. endosomolytic compounds) is crucial. The study hence stresses the importance of selection of appropriate cell culture model, relevant to in vivo target, to assess the gene silencing efficiency and decide which functionalities the ‘stratified siRNA silencing vector’ requires.
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spelling nottingham-353332020-05-04T18:06:23Z https://eprints.nottingham.ac.uk/35333/ Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency Capel, Victoria Vllasaliu, Driton Watts, Peter Stolnik, Snow Despite research efforts, cell uptake processes determining siRNA silencing efficiency remain unclear. Here, we examine the relationship between in vitro cell culture models, cellular trafficking and siRNA silencing efficiency to provide a mechanistic insight on siRNA delivery system design. Model siRNA-polyplexes, based on chitosan as a ‘classical’ condensing agent, were applied to a panel of lung epithelial cell lines, H1299, A549 and Calu-3 and cell internalization levels, trafficking pathways and gene silencing assessed on exposure to pharmacological inhibitors. The data reveal striking differences in the internalization behaviour and gene silencing efficiency in the tested cell lines, despite their common lung epithelial origins. The model system’s silencing was lower where clathrin internalization pathway predominated in Calu-3, relative to silencing in H1299 cells where a non-clathrin internalization appears dominant. Increased silencing on endosomal disruption was apparent in Calu-3 cells, but absent when cellular internalization was not predominantly clathrin-mediated in A549 cells. This highlights that identifying cell trafficking pathways before incorporation of functional components to siRNA delivery systems (e.g. endosomolytic compounds) is crucial. The study hence stresses the importance of selection of appropriate cell culture model, relevant to in vivo target, to assess the gene silencing efficiency and decide which functionalities the ‘stratified siRNA silencing vector’ requires. Elsevier 2016-08-19 Article PeerReviewed Capel, Victoria, Vllasaliu, Driton, Watts, Peter and Stolnik, Snow (2016) Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency. Biochemical and Biophysical Research Communications, 477 (2). pp. 260-265. ISSN 0006-291X Endocytosis pathways; Lung siRNA therapy; Pharmacological inhibitors; siRNA polyplexes; siRNA silencing http://www.sciencedirect.com/science/article/pii/S0006291X1630972X?via%3Dihub doi:10.1016/j.bbrc.2016.06.054 doi:10.1016/j.bbrc.2016.06.054
spellingShingle Endocytosis pathways; Lung siRNA therapy; Pharmacological inhibitors; siRNA polyplexes; siRNA silencing
Capel, Victoria
Vllasaliu, Driton
Watts, Peter
Stolnik, Snow
Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency
title Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency
title_full Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency
title_fullStr Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency
title_full_unstemmed Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency
title_short Insight into the relationship between the cell culture model, cell trafficking and siRNA silencing efficiency
title_sort insight into the relationship between the cell culture model, cell trafficking and sirna silencing efficiency
topic Endocytosis pathways; Lung siRNA therapy; Pharmacological inhibitors; siRNA polyplexes; siRNA silencing
url https://eprints.nottingham.ac.uk/35333/
https://eprints.nottingham.ac.uk/35333/
https://eprints.nottingham.ac.uk/35333/