The potential of antisense oligonucleotide therapies for inherited childhood lung diseases.

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The potential of antisense oligonucleotide therapies for inherited childhood lung diseases.

Antisense oligonucleotides are an emerging therapeutic option to treat diseases with known genetic origin. In the age of personalised medicines, antisense oligonucleotides can sometimes be designed to target and bypass or overcome a patient's genetic mutation, in particular those lesions that c...

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Bibliographic Details
Main Authors:	Martinovich, K., Shaw, N., Kicic, Anthony, Schultz, A., Fletcher, S., Wilton, S., Stick, S.
Format:	Journal Article
Language:	English
Published:	2018
Subjects:	Antisense oligonucleotides Childhood Cystic fibrosis Inherited diseases Surfactant disorders
Online Access:	http://hdl.handle.net/20.500.11937/76807

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