Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective

Due to the remarkable global surge in activity in rare diseases research over the last six years, including contributions by the International Rare Diseases Research Consortium (IRDiRC), the Consortium's 2020 goals have been largely achieved by 2017. Though these developments are gratifying, en...

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Main Authors: Austin, C., Cutillo, C., Lau, L., Jonker, A., Rath, A., Julkowska, D., Thomson, D., Terry, S., de Montleau, B., Ardigò, D., Hivert, V., Boycott, K., Baynam, Gareth, Kaufmann, P., Taruscio, D., Lochmüller, H., Suematsu, M., Incerti, C., Draghia-Akli, R., Norstedt, I., Wang, L., Dawkins, Hugh
Format: Journal Article
Published: 2018
Online Access:http://hdl.handle.net/20.500.11937/72422
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author Austin, C.
Cutillo, C.
Lau, L.
Jonker, A.
Rath, A.
Julkowska, D.
Thomson, D.
Terry, S.
de Montleau, B.
Ardigò, D.
Hivert, V.
Boycott, K.
Baynam, Gareth
Kaufmann, P.
Taruscio, D.
Lochmüller, H.
Suematsu, M.
Incerti, C.
Draghia-Akli, R.
Norstedt, I.
Wang, L.
Dawkins, Hugh
author_facet Austin, C.
Cutillo, C.
Lau, L.
Jonker, A.
Rath, A.
Julkowska, D.
Thomson, D.
Terry, S.
de Montleau, B.
Ardigò, D.
Hivert, V.
Boycott, K.
Baynam, Gareth
Kaufmann, P.
Taruscio, D.
Lochmüller, H.
Suematsu, M.
Incerti, C.
Draghia-Akli, R.
Norstedt, I.
Wang, L.
Dawkins, Hugh
author_sort Austin, C.
building Curtin Institutional Repository
collection Online Access
description Due to the remarkable global surge in activity in rare diseases research over the last six years, including contributions by the International Rare Diseases Research Consortium (IRDiRC), the Consortium's 2020 goals have been largely achieved by 2017. Though these developments are gratifying, enormous challenges remain. With this paradox in mind, IRDiRC set new global rare disease goals for the coming decade with the ultimate aim of improved health for people living with rare diseases worldwide. This article is protected by copyright. All rights reserved.
first_indexed 2025-11-14T10:52:27Z
format Journal Article
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institution Curtin University Malaysia
institution_category Local University
last_indexed 2025-11-14T10:52:27Z
publishDate 2018
recordtype eprints
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spelling curtin-20.500.11937-724222018-12-13T09:33:38Z Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective Austin, C. Cutillo, C. Lau, L. Jonker, A. Rath, A. Julkowska, D. Thomson, D. Terry, S. de Montleau, B. Ardigò, D. Hivert, V. Boycott, K. Baynam, Gareth Kaufmann, P. Taruscio, D. Lochmüller, H. Suematsu, M. Incerti, C. Draghia-Akli, R. Norstedt, I. Wang, L. Dawkins, Hugh Due to the remarkable global surge in activity in rare diseases research over the last six years, including contributions by the International Rare Diseases Research Consortium (IRDiRC), the Consortium's 2020 goals have been largely achieved by 2017. Though these developments are gratifying, enormous challenges remain. With this paradox in mind, IRDiRC set new global rare disease goals for the coming decade with the ultimate aim of improved health for people living with rare diseases worldwide. This article is protected by copyright. All rights reserved. 2018 Journal Article http://hdl.handle.net/20.500.11937/72422 10.1111/cts.12500 restricted
spellingShingle Austin, C.
Cutillo, C.
Lau, L.
Jonker, A.
Rath, A.
Julkowska, D.
Thomson, D.
Terry, S.
de Montleau, B.
Ardigò, D.
Hivert, V.
Boycott, K.
Baynam, Gareth
Kaufmann, P.
Taruscio, D.
Lochmüller, H.
Suematsu, M.
Incerti, C.
Draghia-Akli, R.
Norstedt, I.
Wang, L.
Dawkins, Hugh
Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective
title Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective
title_full Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective
title_fullStr Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective
title_full_unstemmed Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective
title_short Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective
title_sort future of rare diseases research 2017–2027: an irdirc perspective
url http://hdl.handle.net/20.500.11937/72422