Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families

Rett syndrome is a rare neurological disorder affecting girls and usually caused by a mutation on the MECP2 gene. It is estimated that approximately 1,000 girls are born every year in China with Rett syndrome but far fewer have received a diagnosis. Fourteen of 74 Chinese families known to the Inter...

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Main Authors: Lim, F., Downs, Jennepher, Li, Jianghong, Bao, X., Leonard, H.
Format: Journal Article
Published: John Wiley & Sons, Inc. 2012
Subjects:
Online Access:http://hdl.handle.net/20.500.11937/26128
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author Lim, F.
Downs, Jennepher
Li, Jianghong
Bao, X.
Leonard, H.
author_facet Lim, F.
Downs, Jennepher
Li, Jianghong
Bao, X.
Leonard, H.
author_sort Lim, F.
building Curtin Institutional Repository
collection Online Access
description Rett syndrome is a rare neurological disorder affecting girls and usually caused by a mutation on the MECP2 gene. It is estimated that approximately 1,000 girls are born every year in China with Rett syndrome but far fewer have received a diagnosis. Fourteen of 74 Chinese families known to the International Rett Syndrome Phenotype Database participated in this qualitative study. Telephone interviews were conducted in Mandarin to explore pathways to a diagnosis of Rett syndrome in China and associated barriers. Families consulted multiple clinical centers and eventually received a diagnosis at a centrally located hospital. Over the course of this pathway, families encountered lack of knowledge and diagnostic expertise for Rett syndrome at local levels and a heavily over-burdened hospital system. There was a paucity of information available to guide management of this rare disorder after the diagnosis had been received. Our study suggests that the frustrations experienced by families could in part be addressed by the provision of information, education, and training related to Rett syndrome for clinicians, additional resources to allow clinicians to request genetic testing for confirmation of the clinical diagnosis and for information and support services for families.
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spelling curtin-20.500.11937-261282017-09-13T16:07:45Z Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families Lim, F. Downs, Jennepher Li, Jianghong Bao, X. Leonard, H. developing countries Rett syndrome diagnosis qualitative research China Rett syndrome is a rare neurological disorder affecting girls and usually caused by a mutation on the MECP2 gene. It is estimated that approximately 1,000 girls are born every year in China with Rett syndrome but far fewer have received a diagnosis. Fourteen of 74 Chinese families known to the International Rett Syndrome Phenotype Database participated in this qualitative study. Telephone interviews were conducted in Mandarin to explore pathways to a diagnosis of Rett syndrome in China and associated barriers. Families consulted multiple clinical centers and eventually received a diagnosis at a centrally located hospital. Over the course of this pathway, families encountered lack of knowledge and diagnostic expertise for Rett syndrome at local levels and a heavily over-burdened hospital system. There was a paucity of information available to guide management of this rare disorder after the diagnosis had been received. Our study suggests that the frustrations experienced by families could in part be addressed by the provision of information, education, and training related to Rett syndrome for clinicians, additional resources to allow clinicians to request genetic testing for confirmation of the clinical diagnosis and for information and support services for families. 2012 Journal Article http://hdl.handle.net/20.500.11937/26128 10.1002/ajmg.a.34351 John Wiley & Sons, Inc. restricted
spellingShingle developing countries
Rett syndrome
diagnosis
qualitative research
China
Lim, F.
Downs, Jennepher
Li, Jianghong
Bao, X.
Leonard, H.
Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families
title Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families
title_full Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families
title_fullStr Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families
title_full_unstemmed Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families
title_short Barriers to diagnosis of a rare neurological disorder in China - Lived experiences of Rett Syndrome families
title_sort barriers to diagnosis of a rare neurological disorder in china - lived experiences of rett syndrome families
topic developing countries
Rett syndrome
diagnosis
qualitative research
China
url http://hdl.handle.net/20.500.11937/26128