Search Results - Prabhakar, Shilpa
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Long-term therapeutic efficacy of intravenous AAV-mediated hamartin replacement in mouse model of tuberous sclerosis type 1 by Prabhakar, Shilpa, Cheah, Pike See, Zhang, Xuan, Zinter, Max, Gianatasio, Maria, Hudry, Eloise, Bronson, Roderick T, Kwiatkowski, David J, Rachamimov, Anat Stemmer, Maguire, Casey A, Sena-Esteves, Miguel, Tannous, Bakhos A, Breakefield, Xandra O
Published 2019Get full text
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2
Gene replacement therapy in a schwannoma mouse model of neurofibromatosis type 2 by Prabhakar, Shilpa, Beauchamp, Roberta L., Cheah, Pike See, Yoshinaga, Akiko, Haidar, Edwina Abou, Lule, Sevda, Mani, Gayathri, Maalouf, Katia, Stemmer-Rachamimov, Anat, Jung, David H., Welling, D. Bradley, Giovannini, Marco, Plotkin, Scott R., Maguire, Casey A., Ramesh, Vijaya, Breakefield, Xandra O.
Published 2022Get full text
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3
Engineered AAV capsids mediate transduction of murine neurofibroma and sciatic nerve by Abou Haidar, Edwina, Prabhakar, Shilpa, Cheah, Pike See, Hanlon, Killian S., Espinoza, Paula, Crain, Adam V., Patel, Nikita, Radcliff, Greta W., Cheng, Ming, Hernández, Iván Coto, Minderler, Steven, de la Cruz, Demitri, Ng, Carrie, da Hora, Cintia Carla, Charest, Alain, Stemmer-Rachamimov, Anat, Jowett, Nate, Breakefield, Xandra O., Maguire, Casey A.
Published 2025Get full text
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